Perspective on innovative therapies for globoid cell leukodystrophy-Reference-Cited by-同舟云学术

Perspective on innovative therapies for globoid cell leukodystrophy

Published:2016-09-17 Issue:11 Volume:94 Page:1304-1317
ISSN:0360-4012
Container-title:Journal of Neuroscience Research
language:en
Short-container-title:Journal of Neuroscience Research

Author:

Ricca Alessandra¹,Gritti Angela¹

Affiliation:

1. San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Division of Regenerative Medicine, Stem Cells and Gene Therapy; IRCCS San Raffaele Scientific Institute; Milan Italy

Funder

Fondazione Veronesi Post Doctoral Fellowship (to A.R.)

Fondazione Telethon

European Leukodystrophies Association

Publisher

Wiley

Subject

Cellular and Molecular Neuroscience

Reference155 articles.

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2. Inhibition of angiogenesis by beta-galactosylceramidase deficiency in globoid cell leukodystrophy;Belleri;Brain,2013

3. Gene therapy for lysosomal storage disorders: a good start;Biffi;Hum Mol Genet,2015

4. Gene therapy for leukodystrophies;Biffi;Hum Mol Genet,2011a

5. Lentiviral vector common integration sites in preclinical models and a clinical trial reflect a benign integration bias and not oncogenic selection;Biffi;Blood,2011b

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