Successful haploidentical hematopoietic stem cell transplantation for paroxysmal nocturnal hemoglobinuria with severe pancytopenia developed after long‐term aplastic anemia treatment-Reference-Cited by-同舟云学术

Successful haploidentical hematopoietic stem cell transplantation for paroxysmal nocturnal hemoglobinuria with severe pancytopenia developed after long‐term aplastic anemia treatment

Published:2024-04-26 Issue:5 Volume:12 Page:
ISSN:2050-0904
Container-title:Clinical Case Reports
language:en
Short-container-title:Clinical Case Reports

Author:

Sakurai Kazuki¹²^ORCID,Saito Kei¹,Hatta Shunsuke¹,Katsuoka Yuna¹,Meguro Kuniaki¹,Yokoyama Hisayuki¹²,Izumi Toru¹

Affiliation:

1. Department of Hematology National Hospital Organization Sendai Medical Center Sendai Japan

2. Department of Hematology Tohoku University Hospital Sendai Japan

Abstract

Key Clinical MessageHaploidentical hematopoietic stem cell transplantation (HSCT) with posttransplant cyclophosphamide is an alternative treatment for aplastic anemia–paroxysmal nocturnal hemoglobinuria (PNH) syndrome with poor prognostic factors. Ravulizumab treatment for PNH before HSCT might have a beneficial effect.

Publisher

Wiley

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/ccr3.8832

Reference17 articles.

1. Long-term outcome of a randomized controlled study in patients with newly diagnosed severe aplastic anemia treated with antithymocyte globulin and cyclosporine, with or without granulocyte colony-stimulating factor: a Severe Aplastic Anemia Working Party Trial from the European Group of Blood and Marrow Transplantation

2. Advances in Hematopoietic Stem Cell Transplantation for Patients with Paroxysmal Nocturnal Hemoglobinuria

3. Guidelines for the diagnosis and management of aplastic anaemia

4. In vitro and in vivo evidence of PNH cell sensitivity to immune attack after nonmyeloablative allogeneic hematopoietic cell transplantation

5. Allogeneic stem cell transplantation in paroxysmal nocturnal hemoglobinuria