Long-term safety and efficacy of deferasirox in young pediatric patients with transfusional hemosiderosis: Results from a 5­year observational study (ENTRUST)

Author:

Vichinsky Elliott1,El-Beshlawy Amal2,Al Zoebie Azzam3,Kamdem Annie4,Koussa Suzanne5,Chotsampancharoen Thirachit6,Bruederle Andreas7,Gilotti Geralyn8,Han Jackie8,Elalfy Mohsen9

Affiliation:

1. UCSF Benioff Children's Hospital & Research Center Oakland; Oakland California

2. Cairo University; Cairo Egypt

3. Sheikh Khalifa Medical City; Abu Dhabi UAE

4. Centre Hospitalier Intercommunal; Créteil France

5. Chronic Care Center; Hazmieh Lebanon

6. Songklanagarind Hospital; Songkhla Thailand

7. Novartis Pharma AG; Basel Switzerland

8. Novartis Pharmaceuticals; East Hanover New Jersey

9. Ain Shams University; Cairo Egypt

Funder

Novartis Pharmaceuticals Corporation

Publisher

Wiley

Subject

Oncology,Hematology,Pediatrics, Perinatology and Child Health

Reference28 articles.

1. Prevalence of endocrine complications and short stature in patients with thalassaemia major: a multicenter study by the Thalassaemia International Federation (TIF);Sanctis;Pediatr Endocrinol Rev,2004

2. Growth of children with β-thalassemia major;Low;Indian J Pediatr,2005

3. Short stature and failure of pubertal development in thalassaemia major: evidence for hypothalamic neurosecretory dysfunction of growth hormone secretion and defective pituitary gonadotropin secretion;Roth;Eur J Pediatr,1997

4. Novartis Pharmaceuticals UK Ltd Summary of Product Characteristics - EXJADE 125 mg, 250 mg, 500 mg dispersible tablets 2013 http://www.medicines.org.uk/emc/medicine/18805/SPC/

5. Novartis Pharmaceuticals EXJADE® (deferasirox) US Prescribing Information. 2015 http://www.pharma.us.novartis.com/product/pi/pdf/exjade.pdf

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