1. Program in Genomics and Howard Hughes Medical Institute, Center for Life Science, Room CLS15027.1, Children's Hospital Boston, 3 Blackfan Circle, Boston, Massachusetts 02115, USA
2. Research Institute at Nationwide Children's Hospital, Department of Pediatrics, Center in Gene Therapy, Ohio State University College of Medicine, Columbus, Ohio, USA
3. Stem Cell Program and Hematology/Oncology and Howard Hughes Medical Institute, Children's Hospital Boston, Boston, Massachusetts, USA
4. Harvard Stem Cell Institute, Cambridge, Massachusetts, USA
5. Auke Bay Laboratories, Alaska Fisheries Science Center, NOAA Fisheries, Juneau, Alaska, USA
6. Manton Center for Orphan Disease Research, Children's Hospital Boston, Boston, Massachusetts, USA