AAV8-mediated expression of glucocerebrosidase ameliorates the storage pathology in the visceral organs of a mouse model of Gaucher disease-Reference-Cited by-同舟云学术

AAV8-mediated expression of glucocerebrosidase ameliorates the storage pathology in the visceral organs of a mouse model of Gaucher disease

Published:2006 Issue:6 Volume:8 Page:719-729
ISSN:1099-498X
Container-title:The Journal of Gene Medicine
language:en
Short-container-title:J. Gene Med.

Author:

McEachern Kerry Anne,Nietupski Jennifer B.,Chuang Wei-Lien,Armentano Donna,Johnson Jennifer,Hutto Elizabeth,Grabowski Gregory A.,Cheng Seng H.,Marshall John

Publisher

Wiley

Subject

Genetics(clinical),Drug Discovery,Genetics,Molecular Biology,Molecular Medicine

Reference48 articles.

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2. BENEFICIAL EFFECT OF PRE-TRANSPLANT SPLENECTOMY ON DISPLACEMENT BONE MARROW TRANSPLANTATION FOR GAUCHER'S SYNDROME

3. TEN YEARS' EXPERIENCE OF BONE MARROW TRANSPLANTATION FOR GAUCHER DISEASE

4. Sustained therapeutic effects of oral miglustat (Zavesca,N-butyldeoxynojirimycin, OGT 918) in type I Gaucher disease

5. Replacement Therapy for Inherited Enzyme Deficiency — Macrophage-Targeted Glucocerebrosidase for Gaucher's Disease

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