Author:
Mehta Niraj R.,King Sruthi Tallapragada
Reference56 articles.
1. www.rarediseases.org
2. What the Orphan Drug Act Has Done Lately for Children With Rare Diseases: A 10-Year Analysis
3. Nonclinical Safety Studies for the Conduct of Human Clinical Trials and Marketing Authorization for Pharmaceuticals 2010 www.ich.org
4. Preclinical Safety Evaluation of Biotechnology-Derived Pharmaceuticals 2011 www.ich.org
5. The unexpected role of acid sphingomyelinase in cell death and the pathophysiology of common diseases;Smith;FASEB J,2008