mNIS +7 and lower limb function in inotersen treatment of hereditary transthyretin‐mediated amyloidosis-Reference-Cited by-同舟云学术

mNIS +7 and lower limb function in inotersen treatment of hereditary transthyretin‐mediated amyloidosis

Published:2020-08-13 Issue:4 Volume:62 Page:502-508
ISSN:0148-639X
Container-title:Muscle & Nerve
language:en
Short-container-title:Muscle Nerve

Author:

Dyck P. James B.¹^ORCID,Kincaid John C.²,Wiesman Janice F.³,Polydefkis Michael⁴,Litchy William J.¹,Mauermann Michelle L.¹,Ackermann Elizabeth J.⁵,Guthrie Spencer⁶,Pollock Michael⁷,Jung Shiangtung W.⁸,Baker Brenda F.⁸,Dyck Peter J.¹

Affiliation:

1. Department of Neurology Mayo Clinic Rochester Minnesota USA

2. Department of Neurology Indiana University Indianapolis Indiana USA

3. Department of Neurology New York University New York New York USA

4. Department of Neurology Johns Hopkins University Baltimore Maryland USA

5. Otonomy, Inc. San Diego California USA

6. Aurora Bio San Francisco California USA

7. Akcea Therapeutics, Inc. Cambridge Massachusetts USA

8. Ionis Pharmaceuticals, Inc. Carlsbad California USA

Publisher

Wiley

Subject

Physiology (medical),Cellular and Molecular Neuroscience,Neurology (clinical),Physiology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/mus.27022

Reference24 articles.

1. “Red‐flag” symptom clusters in transthyretin familial amyloid polyneuropathy

2. The molecular biology and clinical features of amyloid neuropathy

3. THAOS – The Transthyretin Amyloidosis Outcomes Survey: initial report on clinical manifestations in patients with hereditary and wild-type transthyretin amyloidosis

4. Cardiac phenotype and clinical outcome of familial amyloid polyneuropathy associated with transthyretin alanine 60 variant

5. Transthyretin amyloidosis

Cited by 7 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Anti-MAG neuropathy: historical aspects, clinical-pathological correlations, and considerations for future therapeutical trials;Arquivos de Neuro-Psiquiatria;2024-02-07

2. Peripheral Nervous, Hepatic, and Gastrointestinal Endpoints for AL Amyloidosis Clinical Trials: Report from the Amyloidosis Forum Multi-organ System Working Group;Advances in Therapy;2023-09-02

3. Novel Therapeutic Approaches in Inherited Neuropathies: A Systematic Review;Pharmaceutics;2023-05-30

4. The impact of inotersen on Neuropathy Impairment Score in patients with hereditary transthyretin amyloidosis with polyneuropathy;BMC Neurology;2023-03-17

5. Long‐term treatment effects of inotersen on health‐related quality of life in patients with hATTR amyloidosis with polyneuropathy: Analysis of the open‐label extension of the NEURO‐TTR trial;Muscle & Nerve;2022-08-04