1. University of California San Francisco California USA
2. University of California Los Angeles California USA
3. Lucile Packard Children's Hospital Stanford University School of Medicine Stanford California USA
4. Rocket Pharmaceuticals Inc. Cranbury New Jersey USA
5. Hematología y Hemoterapia Fundación para la investigación Biomédica Hospital Infantil Universitario Niño Jesús (HIUNJ) Madrid Spain
6. Great Ormond Street Hospital and Great Ormond Street Hospital NHS Foundation Trust University College of London, Institute of Child Health London UK
7. Instituto de Investigación Sanitaria Fundación Jiménez Díaz (IIS‐FJD) Hospital Universitario Fundación Jiménez Díaz Madrid Spain