Ethical Perspectives on Treatment Options with Spinal Muscular Atrophy Patients-Reference-Cited by-同舟云学术

Ethical Perspectives on Treatment Options with Spinal Muscular Atrophy Patients

Published:2022-01-25 Issue:3 Volume:91 Page:305-316
ISSN:0364-5134
Container-title:Annals of Neurology
language:en
Short-container-title:Annals of Neurology

Author:

Yeo Crystal J. J.¹²³⁴⁵^ORCID,Simmons Zachary⁶,De Vivo Darryl C.⁷,Darras Basil T.¹

Affiliation:

1. Boston Children's Hospital, Harvard Medical School Boston MA USA

2. School of Medicine, Medical Sciences, and Nutrition University of Aberdeen Aberdeen UK

3. Lee Kong Chian School of Medicine Imperial College London and NTU Singapore Singapore

4. Agency for Science Technology and Research (A*STAR) Singapore Singapore

5. Feinberg School of Medicine Northwestern University Chicago IL USA

6. Penn State Health Milton S. Hershey Medical Center Hershey PA USA

7. Columbia University New York NY USA

Publisher

Wiley

Subject

Neurology (clinical),Neurology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/ana.26299

Reference65 articles.

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2. Spinraza prescribing information. Cambridge MA: Biogen 2016.

3. Zolgensma prescribing information Bannockburn IL: AveXis2019.

4. Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

5. Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls

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