Low-dose suramin in autism spectrum disorder: a small, phase I/II, randomized clinical trial

Author:

Naviaux Robert K.1234,Curtis Brooke5,Li Kefeng12,Naviaux Jane C.16,Bright A. Taylor12,Reiner Gail E.16,Westerfield Marissa7,Goh Suzanne8,Alaynick William A.12,Wang Lin12,Capparelli Edmund V.9,Adams Cynthia10,Sun Ji10,Jain Sonia11,He Feng11,Arellano Deyna A.10,Mash Lisa E.712,Chukoskie Leanne713,Lincoln Alan5,Townsend Jeanne67

Affiliation:

1. The Mitochondrial and Metabolic Disease Center; University of California; San Diego School of Medicine; 214 Dickinson St., Bldg CTF, Rm C102 San Diego 92103-8467 California

2. Department of Medicine; University of California; San Diego School of Medicine; 214 Dickinson St., Bldg CTF, Rm C102 San Diego 92103-8467 California

3. Department of Pediatrics; University of California; San Diego School of Medicine; 214 Dickinson St., Bldg CTF, Rm C102 San Diego 92103-8467 California

4. Department of Pathology; University of California; San Diego School of Medicine; 214 Dickinson St., Bldg CTF, Rm C102 San Diego 92103-8467 California

5. Alliant International University; 10455 Pomerado Road San Diego California 92131

6. Department of Neurosciences; University of California; San Diego School of Medicine; 9500 Gilman Drive. La Jolla CA 92093-0662

7. The Research in Autism and Development Laboratory (RAD Lab); University of California; 9500 Gilman Drive La Jolla CA 92093-0959

8. Pediatric Neurology Therapeutics; 7090 Miratech Dr San Diego CA 92121

9. Department of Pediatrics; and Skaggs School of Pharmacy and Pharmaceutical Sciences; University of California; San Diego School of Medicine; 9500 Gilman Drive La Jolla CA 92093-0657

10. Clinical and Translational Research Institute (CTRI); University of California; San Diego La Jolla CA 92037

11. Department of Family Medicine and Public Health; University of California; San Diego La Jolla CA 92093

12. Department of Psychology; San Diego State University; 5500 Campanile Drive San Diego CA 92182

13. Institute for Neural Computation; University of California; 9500 Gilman Drive La Jolla 92093-0523

Funder

William Wright Family Foundation

UCSD Christini Fund

Autism Research Institute

Lennox Foundation

Gupta Family and Satya Fund

Agrawal Family

N of One Autism Research Foundation

Rodakis Family

Guts Foundation

UCSD Mitochondrial Disease Research Fund

Dr. Elizabeth Mumper Cooper

Daniel and Kelly White Family

Jane Botsford Johnson Foundation

Publisher

Wiley

Subject

Neurology (clinical),General Neuroscience

Reference49 articles.

1. Estimated prevalence of autism and other developmental disabilities following questionnaire changes in the 2014 National Health interview survey;Zablotsky;Natl Health Stat Report,2015

2. Prevalence and Characteristics of Autism Spectrum Disorder Among Children Aged 8 Years-Autism and Developmental Disabilities Monitoring Network, 11 Sites, United States, 2012;Christensen;MMWR Surveill Summ,2016

3. Functional impact of global rare copy number variation in autism spectrum disorders;Pinto;Nature,2010

4. Prevalence of autism spectrum disorder phenomenology in genetic disorders: a systematic review and meta-analysis;Richards;Lancet Psychiatry,2015

5. Autism spectrum disorder genetics: diverse genes with diverse clinical outcomes;Talkowski;Harv Rev Psychiatry,2014

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