1. Children's Hospital of The King's Daughters Norfolk Virginia USA
2. Department of Paediatric Neurology and Nemo Clinical Centre Catholic University Rome Italy
3. Center for Experimental Neurotherapeutics, St. Jude Children's Research Hospital Memphis Tennessee USA
4. Department of Neuropediatrics and Muscle Disorders Medical Center University of Freiburg, Faculty of Medicine Freiburg Germany
5. Departments of Neurology and Pediatrics Columbia University Irving Medical Center New York New York USA
6. The Dubowitz Neuromuscular Centre University College London, Great Ormond Street Institute of Child Health & Great Ormond Street Hospital London UK
7. National Institute of Health Research, Great Ormond Street Hospital Biomedical Research Centre London UK
8. Institute of Medical Genetics, Tokyo Women's Medical University Tokyo Japan
9. Department of Clinical and Molecular Genetics Hospital Vall d'Hebron Barcelona Spain
10. Hôpital Necker Enfants Malades, APHP Paris France
11. Garches Neuromuscular Reference Center (GNMH) APHP Raymond Poincare University Hospital (UVSQ Paris Saclay) Garches France
12. Novartis Gene Therapies Switzerland GmbH Rotkreuz Switzerland
13. Novartis Gene Therapies, Inc Bannockburn Illinois USA
14. Institute for Precision and Individualized Therapy, Eshelman School of Pharmacy, University of North Carolina at Chapel Hill Chapel Hill North Carolina USA
15. Genomics, Biotech and Emerging Medical Technology Institute, National Association of Managed Care Physicians Richmond Virginia USA
16. Department of Paediatrics MDUK Oxford Neuromuscular Centre & NIHR Oxford Biomedical Research Centre University of Oxford Oxford UK
17. Department of Paediatrics, Neuromuscular Reference Center University and University Hospital of Liège Liège Belgium