1. Neuromuscular Diseases Department; University Hospital Pellegrin; Bordeaux France
2. Neuromuscular Diseases Department; University Hospital L'Archet; Nice France
3. Neuromuscular Diseases Department; University Hospital La Timone; Marseille France
4. Market Access and Pricing Department; LFB Biomedicaments; Les Ulis France
5. International Scientific Affairs Unit; LFB Biomedicaments; Les Ulis France
6. Public Health, AP-HP; University Paris Est Creteil, & ECEVE UMR 1123; Paris France