Genetic modifiers of ambulation in the cooperative international Neuromuscular research group Duchenne natural history study-Reference-Cited by-同舟云学术

Genetic modifiers of ambulation in the cooperative international Neuromuscular research group Duchenne natural history study

Published:2015-03-13 Issue:4 Volume:77 Page:684-696
ISSN:0364-5134
Container-title:Annals of Neurology
language:en
Short-container-title:Ann Neurol.

Author:

Bello Luca¹²^ORCID,Kesari Akanchha¹,Gordish‐Dressman Heather¹,Cnaan Avital¹³,Morgenroth Lauren P.¹,Punetha Jaya¹⁴,Duong Tina¹,Henricson Erik K.⁵^ORCID,Pegoraro Elena²,McDonald Craig M.⁵,Hoffman Eric P.¹⁴,

Affiliation:

1. Children's National Medical CenterWashington DC

2. Department of Neuroscience (Neurological, Psychiatric, Sensory, Reconstructive, Rehabilitative Science)University of PaduaPadua Italy

3. Departments of Pediatrics, Epidemiology, and BiostatisticsGeorge Washington UniversityWashington DC

4. Department of Integrative Systems BiologyGeorge Washington UniversityWashington DC

5. Department of Physical Medicine and RehabilitationUniversity of CaliforniaDavis, Sacramento CA

Funder

NIH

US Department of Education/National Institute on Disability and Rehabilitation Research

Publisher

Wiley

Subject

Neurology (clinical),Neurology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/ana.24370

Reference33 articles.

1. Dystrophin: The protein product of the duchenne muscular dystrophy locus

2. Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

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5. Modifying muscular dystrophy through transforming growth factor-β

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