1. Cincinnati Children's Hospital Medical Center Cincinnati Ohio USA
2. Children's Hospital Los Angeles and Keck School of Medicine University of Southern California Los Angeles California USA
3. Great Ormond Street Hospital for Children NHS Foundation Trust London UK
4. Birmingham Children's Hospital NHS Foundation Trust Birmingham UK
5. Texas Children's Hospital Baylor College of Medicine Houston Texas USA
6. Seattle Children's Hospital and University of Washington School of Medicine Seattle Washington USA
7. Shire Human Genetic Therapies, Inc Lexington Massachusetts USA
8. MedStar Georgetown University Hospital Washington District of Columbia USA
9. University of Nebraska Medical Center Omaha Nebraska USA
10. Children's Hospital Pediatric Research Center University of Helsinki, Helsinki University Hospital Helsinki Finland
11. Mattel Children's Hospital UCLA Department of Pediatrics Los Angeles California USA
12. The Hospital for Sick Children Toronto Ontario Canada
13. Shire Human Genetic Therapies, Inc Cambridge Massachusetts USA