Don't Do Different Things…Do Things Differently! Drug Development in Rare Diseases-Reference-Cited by-同舟云学术

Don't Do Different Things…Do Things Differently! Drug Development in Rare Diseases

Published:2016-08-16 Issue:4 Volume:100 Page:333-335
ISSN:0009-9236
Container-title:Clinical Pharmacology & Therapeutics
language:en
Short-container-title:Clin. Pharmacol. Ther.

Author:

Rudek MA¹,Korth-Bradley JM²

Affiliation:

1. Department of Oncology and Department of Medicine, Division of Clinical Pharmacology; The Johns Hopkins University School of Medicine and The Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins; Baltimore Maryland USA

2. Clinical Pharmacology, Rare Diseases, Global Product Development; Pfizer Inc.; Collegeville Pennsylvania USA

Publisher

Wiley

Subject

Pharmacology (medical),Pharmacology

Reference10 articles.

1. Rare disease terminology and definitions - a systematic global review: report of the ISPOR Rare Disease Special Interest Group;Richter;Value Health,2015

2. Incentives for starting small companies focused on rare and neglected diseases;Ekins;Pharm. Res.,2016

3. Challenges and hurdles to business as usual in drug development for treatment of rare diseases;Swinney;Clin. Pharmacol. Ther.,2016

4. Don't do different things - do things differently! Drug development in rare diseases;Speid;Clin. Pharmacol. Ther.,2016

5. A clinical pharmacology-regulatory perspective on the approval of drugs for rare diseases

Cited by 2 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Development and Deployment of Gene Therapies;Second Generation Cell and Gene-based Therapies;2020

2. Challenges and Opportunities in Rare Disease Drug Development;Clinical Pharmacology & Therapeutics;2016-09-09