1. Department of Pediatrics Stanford University School of Medicine Stanford California USA
2. Department of Pediatrics University of California San Diego San Diego California USA
3. Department of Pediatrics University of Utah Salt Lake City Utah USA
4. Oulu University Hospital University of Oulu Oulu Finland
5. Patient Centered Outcomes ICON Gaithersburg Maryland USA
6. Patient Centered Outcomes ICON South San Francisco California USA
7. Global Clinical Development, Rare Metabolic Diseases Takeda Zurich Switzerland
8. Global Clinical Development, Rare Metabolic Diseases Takeda Cambridge Massachusetts USA
9. Global Evidence and Outcomes Takeda Lexington Massachusetts USA