1. Division of Pediatric Hematology Oncology, Children's Hospital Boston, and Dana‐Farber Cancer Institute; Department of Biological Chemistry and Molecular Pharmacology, Harvard Medical School Boston Massachusetts
2. Harvard Stem Cell Institute Cambridge Massachusetts
3. These authors contributed equally to this work and are co‐first authors
4. Howard Hughes Medical Institute Boston Massachusetts
5. Immune Disease Institute, Program in Cellular and Molecular Medicine, Children's Hospital Boston, Harvard Stem Cell Institute, and the Department of Pathology, Harvard Medical School Boston Massachusetts
6. Department of Genetics, Yale Stem Cell Center, Yale University School of Medicine New Haven Connecticut
7. These authors are co‐corresponding authors
8. Division of Hematology, Brigham and Women's Hospital Boston Massachusetts
9. Manton Center for Orphan Disease Research Boston Massachusetts