Myostatin inhibitor ACE-031 treatment of ambulatory boys with Duchenne muscular dystrophy: Results of a randomized, placebo-controlled clinical trial

Author:

Campbell Craig1,McMillan Hugh J.2,Mah Jean K.3,Tarnopolsky Mark4,Selby Kathryn5,McClure Ty6,Wilson Dawn M.6,Sherman Matthew L.6,Escolar Diana7,Attie Kenneth M.6

Affiliation:

1. Pediatrics, Epidemiology and Clinical Neurological Sciences; Western University; London Ontario Canada

2. Children's Hospital of Eastern Ontario; University of Ottawa; Ottawa Ontario Canada

3. Alberta Children's Hospital; University of Calgary; Calgary Alberta Canada

4. McMaster University Medical Centre; Hamilton Ontario Canada

5. British Columbia Children's Hospital; University of British Columbia; Vancouver British Columbia Canada

6. Acceleron Pharma; Cambridge Massachusetts USA

7. Kennedy Krieger Institute; Johns Hopkins Medical School; Baltimore Maryland USA

Publisher

Wiley

Subject

Physiology (medical),Cellular and Molecular Neuroscience,Clinical Neurology,Physiology

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