Clinical Design and Analysis Strategies for the Development of Gene Therapies: Considerations for Quantitative Drug Development in the Age of Genetic Medicine
Author:
Affiliation:
1. Novartis Gene Therapies Bannockburn Illinois USA
2. Novartis Pharmaceuticals Cambridge Massachusetts USA
Publisher
Wiley
Subject
Pharmacology (medical),Pharmacology
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1002/cpt.2224
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1. Engineering adeno-associated virus vectors for gene therapy
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5. Estimating the Clinical Pipeline of Cell and Gene Therapies and Their Potential Economic Impact on the US Healthcare System
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