1. Department of Neurology Boston Children's Hospital and Harvard Medical School Boston Massachusetts
2. Department of Neurology Johns Hopkins University School of Medicine Baltimore Maryland
3. Department of Pediatrics Johns Hopkins University School of Medicine Baltimore Maryland
4. Division of Neurology Department of Pediatrics Nemours Children's Hospital Orlando Florida
5. Department of Paediatric Neurology Catholic University Rome Italy
6. Departments of Neurology and Pediatrics Columbia University Irving Medical Center New York New York
7. Department of Neurology and Neurosurgery and Department of Pediatrics McGill University Montreal Quebec Canada
8. Department of Clinical and Molecular Genetics and Rare Diseases Unit Hospital Vall d′Hebron and Centro de Investigacíon Biomédica en Red Enfermedades Raras (CIBERER) Barcelona Spain
9. Royal Children's Hospital Murdoch Children's Research Institute and University of Melbourne Melbourne Australia
10. Dubowitz Neuromuscular Centre University College London London United Kingdom
11. NIHR Great Ormond Street Hospital Biomedical Research Centre London United Kingdom
12. Biogen Cambridge Massachusetts
13. Department of Neuroscience Johns Hopkins University School of Medicine Baltimore Maryland