Randomized phase 2 study of ACE ‐083, a muscle‐promoting agent, in facioscapulohumeral muscular dystrophy

Author:

Statland Jeffrey M.1ORCID,Campbell Craig2,Desai Urvi3,Karam Chafic4,Díaz‐Manera Jordi567ORCID,Guptill Jeffrey T.8,Korngut Lawrence9,Genge Angela10,Tawil Rabi N.11,Elman Lauren12,Joyce Nanette C.13,Wagner Kathryn R.14,Manousakis Georgios15ORCID,Amato Anthony A.16,Butterfield Russell J.17ORCID,Shieh Perry B.18ORCID,Wicklund Matthew19,Gamez Josep20ORCID,Bodkin Cynthia21,Pestronk Alan22,Weihl Conrad C.22,Vilchez‐Padilla Juan J.2324,Johnson Nicholas E.25ORCID,Mathews Katherine D.26,Miller Barry27,Leneus Ashley27,Fowler Marcie27,van de Rijn Marc27,Attie Kenneth M.27

Affiliation:

1. Department of Neurology University of Kansas Medical Center Kansas City Kansas USA

2. Department of Pediatrics and Clinical Neurological Sciences University of Western Ontario London Ontario Canada

3. Carolinas MDA Care Center Atrium Health Charlotte North Carolina USA

4. Neuromuscular Division Oregon Health & Science University Portland Oregon USA

5. Neuromuscular Diseases Unit, Neurology Department Hospital de la Santa Creu I Sant Pau Barcelona Spain

6. Instituto de Salud Carlos III Centro de Investigación Biomédica en Red de Enfermedades Raras Madrid Spain

7. John Walton Muscular Dystrophy Research Centre Newcastle University Translational and Clinical Research Institute Newcastle UK

8. Department of Neurology Duke University School of Medicine Durham North Carolina USA

9. University of Calgary Calgary Alberta Canada

10. Montreal Neurological Institute Montreal Quebec Canada

11. University of Rochester School of Medicine Rochester New York USA

12. University of Pennsylvania Philadelphia Pennsylvania USA

13. University of California Davis Medical Center Davis California USA

14. Johns Hopkins School of Medicine Kennedy Krieger Institute Baltimore Maryland USA

15. Department of Neurology University of Minnesota Minneapolis Minnesota USA

16. Brigham and Women's Hospital Boston Massachusetts USA

17. Departments of Neurology and Pediatrics University of Utah Salt Lake City Utah USA

18. University of California Los Angeles Los Angeles California USA

19. University of Colorado Aurora Colorado USA

20. Department of Medicine, GMA Clinic European Reference Network on Rare Neuromuscular Diseases (ERN EURO‐NMD) and Universitat Autònoma de Barcelona Barcelona Spain

21. Indiana University School of Medicine Indianapolis Indiana USA

22. Washington University School of Medicine St. Louis Missouri USA

23. Hospital UIP La Fe Neuromuscular Reference Centre Valencia Spain

24. Instituto de Salud Carlos III, Centro de Investigación Biomédica en Red de Enfermedades Raras Madrid Spain

25. Virginia Commonwealth University Richmond Virginia USA

26. Carver College of Medicine University of Iowa Iowa City Iowa USA

27. Acceleron Pharma Cambridge Massachusetts USA

Funder

Acceleron

Publisher

Wiley

Subject

Physiology (medical),Cellular and Molecular Neuroscience,Neurology (clinical),Physiology

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