Rescue of cardiomyopathy through U7sn RNA ‐mediated exon skipping in Mybpc3 ‐targeted knock‐in mice-Reference-Cited by-同舟云学术

Rescue of cardiomyopathy through U7sn RNA ‐mediated exon skipping in Mybpc3 ‐targeted knock‐in mice

Published:2013-05-29 Issue:7 Volume:5 Page:1128-1145
ISSN:1757-4676
Container-title:EMBO Molecular Medicine
language:en
Short-container-title:EMBO Mol Med

Author:

Gedicke‐Hornung Christina¹²,Behrens‐Gawlik Verena¹²,Reischmann Silke¹²,Geertz Birgit¹²,Stimpel Doreen¹²,Weinberger Florian¹²,Schlossarek Saskia¹²,Précigout Guillaume³⁴,Braren Ingke¹²⁵,Eschenhagen Thomas¹²,Mearini Giulia¹²,Lorain Stéphanie³⁴,Voit Thomas³⁴,Dreyfus Patrick A.³⁴,Garcia Luis³⁴,Carrier Lucie¹²³⁴

Affiliation:

1. Department of Experimental Pharmacology and ToxicologyCardiovascular Research Center, University Medical Center Hamburg‐EppendorfHamburgGermany

2. DZHK (German Centre for Cardiovascular Research)partner site Hamburg/Kiel/LübeckGermany

3. Inserm U974, CNRS UMR7215Institut de MyologieParisFrance

4. Pierre and Marie Curie University ParisParisFrance

5. Hamburg Zentrum für Experimentelle Therapieforschung (HEXT) Vector Core Unit, Department of Experimental Pharmacology and ToxicologyUniversity Medical Center Hamburg‐EppendorfHamburgGermany

Publisher

EMBO

Subject

Molecular Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/emmm.201202168

Reference61 articles.

1. Antisense-Induced Multiexon Skipping for Duchenne Muscular Dystrophy Makes More Sense

2. Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy

3. Antisense-mediated exon skipping: A versatile tool with therapeutic and research applications

4. MRI roadmap-guided transendocardial delivery of exon-skipping recombinant adeno-associated virus restores dystrophin expression in a canine model of Duchenne muscular dystrophy

5. Phosphorylation and function of cardiac myosin binding protein-C in health and disease

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