Effective delivery of large genes to the retina by dual AAV vectors-Reference-Cited by-同舟云学术

Effective delivery of large genes to the retina by dual AAV vectors

Published:2013-12-16 Issue:2 Volume:6 Page:194-211
ISSN:1757-4676
Container-title:EMBO Molecular Medicine
language:en
Short-container-title:EMBO Mol Med

Author:

Trapani Ivana¹,Colella Pasqualina¹,Sommella Andrea¹,Iodice Carolina¹,Cesi Giulia¹,Simone Sonia¹,Marrocco Elena¹,Rossi Settimio²,Giunti Massimo³,Palfi Arpad⁴,Farrar Gwyneth J⁴,Polishchuk Roman¹,Auricchio Alberto¹⁵

Affiliation:

1. Telethon Institute of Genetics and Medicine (TIGEM) Naples Italy

2. Department of Ophthalmology Second University of Naples Naples Italy

3. Department of Veterinary Morphophysiology and Animal Production University of Bologna Bologna Italy

4. The School of Genetics & Microbiology Trinity College Dublin Dublin Ireland

5. Medical Genetics Department of Translational Medicine Federico II University Naples Italy

Publisher

EMBO

Subject

Molecular Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/emmm.201302948

Reference79 articles.

1. Correction: Corrigendum: A photoreceptor cell-specific ATP-binding transporter gene (ABCR) is mutated in recessive Stargardt macular dystrophy

2. Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice

3. Novel Adeno-Associated Virus Serotypes Efficiently Transduce Murine Photoreceptors

4. Fighting Blindness with Adeno-Associated Virus Serotype 8

5. Isolation of Highly Infectious and Pure Adeno-Associated Virus Type 2 Vectors with a Single-Step Gravity-Flow Column

Cited by 203 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. In vivo liver targeted genome editing as therapeutic approach: progresses and challenges;Frontiers in Genome Editing;2024-08-23

2. The ABCs of Stargardt disease: the latest advances in precision medicine;Cell & Bioscience;2024-07-26

3. Recovery kinetics of dual AAV-mediated human otoferlin expression;Frontiers in Molecular Neuroscience;2024-06-17

4. Pluripotent stem cell-derived models of retinal disease: Elucidating pathogenesis, evaluating novel treatments, and estimating toxicity;Progress in Retinal and Eye Research;2024-05

5. Centring equity in the response to chronic suppurative otitis media;The Lancet;2024-05