Liver gene therapy by lentiviral vectors reverses anti‐factor IX pre‐existing immunity in haemophilic mice-Reference-Cited by-同舟云学术

Liver gene therapy by lentiviral vectors reverses anti‐factor IX pre‐existing immunity in haemophilic mice

Published:2013-09-16 Issue:11 Volume:5 Page:1684-1697
ISSN:1757-4676
Container-title:EMBO Molecular Medicine
language:en
Short-container-title:EMBO Mol Med

Author:

Annoni Andrea¹,Cantore Alessio¹²,Della Valle Patrizia³,Goudy Kevin¹,Akbarpour Mahzad¹²,Russo Fabio¹,Bartolaccini Sara¹,D'Angelo Armando³,Roncarolo Maria Grazia¹²,Naldini Luigi¹²

Affiliation:

1. TIGET, San Raffaele Telethon Institute for Gene TherapySan Raffaele Scientific InstituteMilanItaly

2. Vita Salute San Raffaele UniversityMilanItaly

3. Coagulation Service and Thrombosis Research UnitSan Raffaele Scientific InstituteMilanItaly

Publisher

EMBO

Subject

Molecular Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/emmm.201302857

Reference38 articles.

1. In vivo delivery of a microRNA-regulated transgene induces antigen-specific regulatory T cells and promotes immunologic tolerance

2. Inhibitor Development

3. Clinical issues in inhibitors

4. Immune tolerance induction in patients with severe hemophilia with inhibitors: expert panel views and recommendations for clinical practice

5. Modern haemophilia care

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