Novel outcome measures for clinical trials in cystic fibrosis-Reference-Cited by-同舟云学术

Novel outcome measures for clinical trials in cystic fibrosis

Published:2014-12-30 Issue:3 Volume:50 Page:302-315
ISSN:8755-6863
Container-title:Pediatric Pulmonology
language:en
Short-container-title:Pediatr Pulmonol.

Author:

Tiddens Harm A.W.M.¹,Puderbach Michael²,Venegas Jose G.³,Ratjen Felix⁴,Donaldson Scott H.⁵,Davis Stephanie D.⁶,Rowe Steven M.⁷,Sagel Scott D.⁸,Higgins Mark⁹,Waltz David A.¹⁰

Affiliation:

1. Department of Pediatric Pulmonology and AllergologyDepartment of RadiologyErasmus University Medical Center‐Sophia Children's HospitalRotterdamThe Netherlands

2. Department for Diagnostic and Interventional RadiologyHufeland KlinikumBad LangensalzaGermany

3. Department of Anesthesia, Critical Care and Pain MedicineMassachusetts General HospitalBostonMassachusetts

4. Department of PediatricsDivision of Respiratory MedicineHospital for Sick ChildrenUniversity of TorontoTorontoOntario

5. Department of MedicineUniversity of North CarolinaChapel HillNorth Carolina

6. Department of PediatricsJames Whitcomb Riley Hospital for ChildrenIndiana University School of MedicineIndianapolisIndiana

7. Department of MedicineUniversity of Alabama at BirminghamBirminghamAlabama

8. Department of PediatricsChildren's Hospital ColoradoUniversity of Colorado School of MedicineDenverColorado

9. Vertex Pharmaceuticals EuropeAbingdonUK

10. Vertex PharmaceuticalsBostonMassachusetts

Funder

Novartis Pharma AG

Publisher

Wiley

Subject

Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/ppul.23146

Reference149 articles.

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2. Use of Lung Imaging Studies as Outcome Measures for Development of New Therapies in Cystic Fibrosis

3. A new model for cystic fibrosis management: control concept;Yuksel H;Pneumologia,2011

4. Lung Clearance Index at 4 Years Predicts Subsequent Lung Function in Children with Cystic Fibrosis

5. A CFTR Potentiator in Patients with Cystic Fibrosis and theG551DMutation

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