Toward therapy for DYT1 dystonia: Allele-specific silencing of mutant TorsinA
Author:
Publisher
Wiley
Subject
Clinical Neurology,Neurology
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4. Mutant Allele-Specific CRISPR Disruption in DYT1 Dystonia Fibroblasts Restores Cell Function;Molecular Therapy - Nucleic Acids;2020-09
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