Ataluren and similar compounds (specific therapies for premature termination codon class I mutations) for cystic fibrosis

Author:

Aslam Aisha A1,Higgins Colin2,Sinha Ian P1,Southern Kevin W1

Affiliation:

1. University of Liverpool; Department of Women's and Children's Health; Alder Hey Children's NHS Foundation Trust Eaton Road Liverpool UK L12 2AP

2. Alder Hey Children's NHS Foundation Trust; Eaton Road Liverpool UK L12 2AP

Publisher

Wiley

Subject

Pharmacology (medical)

Reference53 articles.

1. The use of high resolution computerized tomography of the chest in evaluating the effect of ataluren in nonsense mutation cystic fibrosis (nmCF) lung disease [abstract];Ajayi;Journal of Cystic Fibrosis,2013

2. Ataluren in nonsense mutation cystic fibrosis patients not receiving tobramycin: significant lung function benefits in the paediatric age range;Davies;Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society,2016

3. Ataluren significantly reduces exacerbations in nonsense mutation cystic fibrosis patients not receiving tobramycin;Boeck;Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society,2016

4. Design of the ataluren confirmatory phase 3, randomised, double-blind, placebo-controlled trial in patients with nonsense mutation cystic fibrosis (ACT CF) [abstract];DeBoeck;Pediatric Pulmonology,2014

5. Ataluren for the treatment of nonsense-mutation cystic fibrosis: A randomised, double-blind, placebo-controlled phase 3 trial;Kerem;The Lancet. Respiratory Medicine,2014

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