Deferiprone (GPO-L-ONE®) monotherapy reduces iron overload in transfusion-dependent thalassemias: 1-year results from a multicenter prospective, single arm, open label, dose escalating phase III pediatric study (GPO-L-ONE; A001) from Thailand

Author:

Viprakasit Vip1,Nuchprayoon Issarang2,Chuansumrit Ampaiwan3,Torcharus Kitti4,Pongtanakul Bunchoo1,Laothamatas Jiraporn5,Srichairatanakool Somdet6,Pooliam Julaporn7,Supajitkasem Siriwat8,Suriyaphol Prapat8,Tanphaichitr Voravarn S.19,Tuchinda Soodsarkorn9

Affiliation:

1. Hematology/Oncology Division, Department of Pediatrics and Thalassemia Center; Faculty of Medicine Siriraj Hospital, Mahidol University; Bangkok Thailand

2. Department of Pediatrics; King Chulalongkorn Memorial Hospital, Chulalongkorn University; Bangkok Thailand

3. Department of Pediatrics; Ramathibodi Hospital, Mahidol University; Bangkok Thailand

4. Department of Pediatrics; Phramongkutklao College of Medicine; Bangkok Thailand

5. Department of Radiology; Ramathibodi Hospital, Mahidol University; Bangkok Thailand

6. Department of Biochemistry; Faculty of Medicine; Chiang Mai University; Chiang Mai, Bangkok Thailand

7. Clinical Epidemiology Unit, Office for Research and Development, Faculty of Medicine Siriraj Hospital; Mahidol University; Bangkok Thailand

8. Bioinformatics and Data Management for Research Unit; Office for Research and Development, Faculty of Medicine Siriraj Hospital, Mahidol University; Bangkok Thailand

9. Thalassemia Foundation of Thailand (TFT); Bangkok Thailand

Publisher

Wiley

Subject

Hematology

Reference59 articles.

1. Late effects of bone marrow transplantation for thalassemia;Piga;Ann N Y Acad Sci,1998

2. HLA-matched sibling bone marrow transplantation for beta-thalassemia major;Sabloff;Blood,2011

3. Linear growth in homozygous beta-thalassemia and beta-thalassemia/hemoglobin E patients under different treatment regimens;Viprakasit;J Med Assoc Thai,2001

4. Survival and causes of death in thalassaemia major;Zurlo;Lancet,1989

5. Iron-chelating therapy and the treatment of thalassemia;Olivieri;Blood,1997

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