Development of a small molecule that corrects misfolding and increases secretion of Z α 1 ‐antitrypsin

Author:

Lomas David A1ORCID,Irving James A1ORCID,Arico‐Muendel Christopher2,Belyanskaya Svetlana2,Brewster Andrew3,Brown Murray3,Chung Chun‐wa3,Dave Hitesh3,Denis Alexis4,Dodic Nerina4,Dossang Anthony3,Eddershaw Peter3,Klimaszewska Diana3,Haq Imran1,Holmes Duncan S3,Hutchinson Jonathan P3,Jagger Alistair M1,Jakhria Toral3,Jigorel Emilie4,Liddle John3,Lind Ken2,Marciniak Stefan J5,Messer Jeff2,Neu Margaret3,Olszewski Allison2,Ordonez Adriana5,Ronzoni Riccardo1ORCID,Rowedder James3,Rüdiger Martin3,Skinner Steve2,Smith Kathrine J3,Terry Rebecca3,Trottet Lionel4,Uings Iain3,Wilson Steve3,Zhu Zhengrong2,Pearce Andrew C3ORCID

Affiliation:

1. UCL Respiratory Rayne Institute University College London London UK

2. GlaxoSmithKline Cambridge MA USA

3. GlaxoSmithKline Stevenage UK

4. GlaxoSmithKline Paris France

5. Cambridge Institute for Medical Research Cambridgem UK

Funder

GlaxoSmithKline

Medical Research Council

UCLH Biomedical Research Centre

Biotechnology and Biological Sciences Research Council

Publisher

EMBO

Subject

Molecular Medicine

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