Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next‐generation human artificial chromosomes for Duchenne muscular dystrophy-Reference-Cited by-同舟云学术

Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next‐generation human artificial chromosomes for Duchenne muscular dystrophy

Published:2017-12-14 Issue:2 Volume:10 Page:254-275
ISSN:1757-4676
Container-title:EMBO Molecular Medicine
language:en
Short-container-title:EMBO Mol Med

Author:

Benedetti Sara¹²,Uno Narumi³⁴,Hoshiya Hidetoshi¹,Ragazzi Martina¹,Ferrari Giulia¹,Kazuki Yasuhiro³⁴,Moyle Louise Anne¹,Tonlorenzi Rossana⁵,Lombardo Angelo⁶,Chaouch Soraya⁷,Mouly Vincent⁷,Moore Marc⁸,Popplewell Linda⁸,Kazuki Kanako⁴,Katoh Motonobu⁴,Naldini Luigi⁹^ORCID,Dickson George⁸,Messina Graziella⁹,Oshimura Mitsuo⁴,Cossu Giulio¹⁰^ORCID,Tedesco Francesco Saverio¹^ORCID

Affiliation:

1. Department of Cell and Developmental Biology University College London London UK

2. Great Ormond Street Institute of Child Health University College London London UK

3. Department of Biomedical Science Institute of Regenerative Medicine and Biofunction Tottori University Yonago, Tottori Japan

4. Chromosome Engineering Research Center (CERC) Tottori University Yonago, Tottori Japan

5. Division of Neuroscience Institute of Experimental Neurology San Raffaele Scientific Institute Milan Italy

6. San Raffaele Telethon Institute for Gene Therapy (TIGET) San Raffaele Scientific Institute and Vita Salute San Raffaele University Milan Italy

7. AIM/AFM Center for Research in Myology Sorbonne Universités, UPMC Univ. Paris 06, INSERM UMRS974, CNRS FRE3617 Paris France

8. School of Biological Sciences Royal Holloway‐University of London Egham Surrey UK

9. Department of Biosciences University of Milan Milan Italy

10. Division of Cell Matrix Biology and Regenerative Medicine University of Manchester Manchester UK

Funder

Duchenne Parent Project

Biotechnology and Biological Sciences Research Council

Muscular Dystrophy UK

National Institute for Health Research

Japan Society for the Promotion of Science

Medical Research Council

Fondazione Telethon

H2020 European Research Council

Seventh Framework Programme

Fundació la Marató de TV3

Core Research for Evolutional Science and Technology

Publisher

EMBO

Subject

Molecular Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.15252/emmm.201607284

Reference84 articles.

1. Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations

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3. Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters

4. Repair or replace? Exploiting novel gene and cell therapy strategies for muscular dystrophies

5. Progress and prospects of gene therapy clinical trials for the muscular dystrophies

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