Novel AAV capsids for intravitreal gene therapy of photoreceptor disorders

Author:

Pavlou Marina12,Schön Christian2,Occelli Laurence M3,Rossi Axel4,Meumann Nadja45,Boyd Ryan F6,Bartoe Joshua T6,Siedlecki Jakob1,Gerhardt Maximilian J1,Babutzka Sabrina12,Bogedein Jacqueline12,Wagner Johanna E2,Priglinger Siegfried G1,Biel Martin2,Petersen‐Jones Simon M3,Büning Hildegard45ORCID,Michalakis Stylianos12ORCID

Affiliation:

1. Department of Ophthalmology Ludwig‐Maximilians‐University Munich Germany

2. Centre for Integrated Protein Science Munich (CIPSM) at the Department of Pharmacy Ludwig‐Maximilians‐University Munich Germany

3. Department of Small Animal Clinical Sciences Michigan State University East Lansing MI USA

4. Laboratory for Infection Biology and Gene Transfer Institute of Experimental Haematology Hannover Medical School Hannover Germany

5. REBIRTH Research Centre for Translational Regenerative Medicine Hannover Medical School Hannover Germany

6. Ophthalmology Services Charles River Laboratories Mattawan MI USA

Funder

Deutsche Forschungsgemeinschaft

Publisher

EMBO

Subject

Molecular Medicine

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