Natural history study of factor IX deficiency with focus on treatment and complications (B‐Natural)

Author:

Shapiro Amy D.1ORCID,Ragni Margaret V.2ORCID,Borhany Munira3ORCID,Abajas Yasmina L.4,Tarantino Michael D.5ORCID,Holstein Katharina6,Croteau Stacy E.7ORCID,Liesner Riana8ORCID,Tarango Cristina9ORCID,Carvalho Manuela10,McGuinn Catherine11ORCID,Funding Eva12,Kempton Christine L.13ORCID,Bidlingmaier Christoph14,Cohen Alice15,Oldenburg Johannes16ORCID,Kearney Susan17,Knoll Christine18,Kuriakose Philip19,Acharya Suchitra20,Reiss Ulrike M.21ORCID,Kulkarni Roshni22ORCID,Witkop Michelle23ORCID,Lethagen Stefan24,Donfield Sharyne25,LeBeau Petra25,Berntorp Erik26ORCID,Astermark Jan2728ORCID

Affiliation:

1. Indiana Hemophilia and Thrombosis Center Indianapolis IN USA

2. Hemophilia Center of Western Pennsylvania University of Pittsburgh Pittsburgh PA USA

3. National Institute of Blood Disease and Bone Marrow Transplantation Karachi Pakistan

4. Hemophilia and Thrombosis Center University of North Carolina Chapel Hill NC USA

5. Bleeding and Clotting Disorders Institute Peoria IL USA

6. Medical Department Haemophilia Center University Medical Center Hamburg‐Eppendorf Hamburg Germany

7. Boston Hemophilia Center Boston Children's Hospital Boston MA USA

8. Great Ormond Street Hospital for Children NHS Trust supported by NIHR GOSH BRC London UK

9. Department of Pediatrics Cancer and Blood Diseases Institute Cincinnati Children's Hospital Medical Center University of Cincinnati College of Medicine Cincinnati OH USA

10. Congenital Coagulopathies Reference Centre Centro Hospitalar Universitário São João Porto Portugal

11. Weill Cornell Medical College New York NY USA

12. Department of Hematology University Hospital Rigshospitalet Institute of Clinical Medicine University of Copenhagen Copenhagen Denmark

13. Emory University School of Medicine Emory University Atlanta GA USA

14. Dr. v. Hauner’s Childrens University Hospital Hemophilia Center LMU Hospital Munich Germany

15. Newark Beth Israel Medical Center Newark NJ USA

16. University Clinic Bonn Bonn Germany

17. Children's Minnesota Center for Bleeding and Clotting Disorders Minneapolis MN USA

18. Phoenix Children’s Hospital Phoenix AZ USA

19. Henry Ford Hospital Detroit MI USA

20. Northwell Hemostasis and Thrombosis Center New York NY USA

21. St. Jude Children’s Research Hospital Memphis TN USA

22. Michigan State University East Lansing MI USA

23. Northern Regional Bleeding Disorders Center Munson Medical Center Traverse City MI USA

24. Sobi Stockholm Sweden

25. Rho, Inc. Durham NC USA

26. Clinical Coagulation Research Department of Translational Medicine Lund University Malmö Sweden

27. Department of Translational Medicine Lund University Malmö Sweden

28. Department of Hematology, Oncology and Radiation Physics Skåne University Hospital Malmö Sweden

Funder

Biogen

Swedish Orphan Biovitrum

Publisher

Wiley

Subject

Genetics (clinical),Hematology,General Medicine

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