1. Division of Hematology Massachusetts General Hospital Harvard Medical School BostonMAUSA
2. Dana‐Farber/Boston Children’s Cancer and Blood Disorders Center Harvard Medical School Boston MAUSA
3. Lucile Packard Children’s Hospital Stanford University Palo Alto CAUSA
4. Central Pennsylvania Clinic for Special Children & Adults Belleville PAUSA
5. Lancaster General Hospital Lancaster PAUSA
6. Department of Pediatrics Emory University School of Medicine Atlanta GAUSA
7. Aflac Cancer and Blood Disorders Center Children’s Healthcare of Atlanta Atlanta GAUSA
8. Ann & Robert H. Lurie Children’s Hospital of Chicago Chicago IL USA
9. University of TorontoUniversity Health Network Toronto ON Canada
10. Children’s Hospital of MichiganWayne State University School of Medicine Detroit MIUSA
11. DDC Clinic for Special Needs Children Middlefield OHUSA
12. Duke University Medical Center Durham NCUSA
13. Children's Hospital of Pennsylvania and Perelman School of Medicine of the University of Pennsylvania Philadelphia PAUSA
14. Agios Pharmaceuticals Cambridge MA USA