Inhibitor development in previously untreated patients with severe haemophilia: A comparison of included patients and outcomes between a clinical study and a registry‐based study-Reference-Cited by-同舟云学术

Inhibitor development in previously untreated patients with severe haemophilia: A comparison of included patients and outcomes between a clinical study and a registry‐based study

Published:2020-07-06 Issue:5 Volume:26 Page:809-816
ISSN:1351-8216
Container-title:Haemophilia
language:en
Short-container-title:Haemophilia

Author:

Jonker Carla J.¹²^ORCID,Oude Rengerink Katrien¹²^ORCID,Hoes Arno W.²^ORCID,Mol Peter G. M.¹³^ORCID,Berg H. Marijke⁴^ORCID

Affiliation:

1. Dutch Medicines Evaluation Board (CBG‐MEB) Utrecht The Netherlands

2. Julius Center for Health Sciences and Primary Care University Medical Center Utrecht Utrecht The Netherlands

3. Department of Clinical Pharmacy and Pharmacology University Medical Center Groningen Groningen The Netherlands

4. PedNet Haemophilia Research foundation Baarn The Netherlands

Publisher

Wiley

Subject

Genetics(clinical),Hematology,General Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/hae.14100

Reference25 articles.

1. Characteristics of Clinical Trials to Support Approval of Orphan vs Nonorphan Drugs for Cancer

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4. Barriers and Opportunities for Use of Patient Registries in Medicines Regulation

5. Patient Registries: An Underused Resource for Medicines Evaluation

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