Apoptotic effects of platelet factor VIII on megakaryopoiesis: implications for a modified human FVIII for platelet-based gene therapy-Reference-Cited by-同舟云学术

Apoptotic effects of platelet factor VIII on megakaryopoiesis: implications for a modified human FVIII for platelet-based gene therapy

Published:2014-11-04 Issue:12 Volume:12 Page:2102-2112
ISSN:1538-7933
Container-title:Journal of Thrombosis and Haemostasis
language:en
Short-container-title:J Thromb Haemost

Author:

Greene T. K.¹,Lyde R. B.²,Bailey S. C.¹,Lambert M. P.¹³,Zhai L.¹,Sabatino D. E.¹³,Camire R. M.¹³,Arruda V. R.¹³,Poncz M.¹³

Affiliation:

1. Division of Hematology; The Children's Hospital of Philadelphia; Philadelphia PA USA

2. Division of Pharmacology; School of Medicine; University of Pennsylvania; Philadelphia PA USA

3. Division of Pediatrics; School of Medicine; University of Pennsylvania; Philadelphia PA USA

Funder

National Institute of Health

Fred Hutchinson Cancer Research Center

Publisher

Wiley

Subject

Hematology

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/jth.12749/fullpdf

Reference37 articles.

1. Advances toward gene therapy for hemophilia at the millennium;Kaufman;Hum Gene Ther,1999

2. Department of Health and Human Services: National Heart LaBRS Pilot study of hemophilia treatment in the US National Heart, Lung and Blood Resources Studies Vol. 3 1972

3. A multicenter study of recombinant factor VIII (recombinate): safety, efficacy, and inhibitor risk in previously untreated patients with hemophilia A. The Recombinate Study Group;Bray;Blood,1994

4. Recombinant factor VIII for the treatment of previously untreated patients with hemophilia A. Safety, efficacy, and development of inhibitors. Kogenate Previously Untreated Patient Study Group;Lusher;N Engl J Med,1993

5. Rational design of a fully active, long-acting PEGylated factor VIII for hemophilia A treatment;Mei;Blood,2010

Cited by 20 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Hematopoietic Stem Cell-Based Platelet-Targeted Gene Therapy for Hemophilia;Comprehensive Hematology and Stem Cell Research;2024

2. Enhancing therapeutic efficacy of in vivo platelet-targeted gene therapy in hemophilia A mice;BLOOD ADV;2020

3. Translational Potential of Immune Tolerance Induction by AAV Liver-Directed Factor VIII Gene Therapy for Hemophilia A;Frontiers in Immunology;2020-04-28

4. Platelet-inspired therapeutics: current status, limitations, clinical implications, and future potential;Drug Delivery and Translational Research;2020-04-22

5. Infused factor VIII–expressing platelets or megakaryocytes as a novel therapeutic strategy for hemophilia A;Blood Advances;2019-04-29