Hemophagocytic lymphohistiocytosis following gene replacement therapy in a child with type 1 spinal muscular atrophy-Reference-Cited by-同舟云学术

Hemophagocytic lymphohistiocytosis following gene replacement therapy in a child with type 1 spinal muscular atrophy

Published:2022-08-04 Issue:9 Volume:47 Page:1478-1481
ISSN:0269-4727
Container-title:Journal of Clinical Pharmacy and Therapeutics
language:en
Short-container-title:Clinical Pharmacy Therapeu

Author:

Galletta Francesca¹^ORCID,Cucinotta Ugo¹,Marseglia Lucia¹,Cacciola Annalisa¹,Gallizzi Romina²,Cuzzocrea Salvatore³,Messina Sonia⁴,Toscano Antonio⁴,Gitto Eloisa¹

Affiliation:

1. Neonatal and Pediatric Intensive Care Unit, University of Messina, Messina, Italy, Department of Human Pathology in Adult and Developmental Age University of Messina Messina Italy

2. Pediatric Unit, Department of Medical of Health Sciences Magna Graecia University Catanzaro Italy

3. Department of Chemical, Biological, Pharmaceutical and Environmental Sciences University of Messina Messina Italy

4. Unit of Neurology and Neuromuscular Diseases, Department of Clinical and Experimental Medicine University of Messina Messina Italy

Publisher

Hindawi Limited

Subject

Pharmacology (medical),Pharmacology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/jcpt.13733

Reference24 articles.

1. Spinal muscular atrophy

2. Spinal Muscular Atrophy

3. Spinal muscular atrophy

4. PSY27 - SPINAL MUSCULAR ATROPHY: A REVIEW OF EPIDEMIOLOGY, BURDEN AND UNMET NEEDS

5. Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy

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