Sometimes they come back: New and old spinal muscular atrophy adults in the era of nusinersen-Reference-Cited by-同舟云学术

Sometimes they come back: New and old spinal muscular atrophy adults in the era of nusinersen

Published:2020-10-31 Issue:2 Volume:28 Page:602-608
ISSN:1351-5101
Container-title:European Journal of Neurology
language:en
Short-container-title:Eur J Neurol

Author:

Sansone V. A.¹,Coratti G.²³,Pera M. C.²³,Pane M.²³,Messina S.⁴⁵,Salmin F.¹,Albamonte E.¹,De Sanctis R.³,Sframeli M.⁵,Di Bella V.⁵,Morando S.⁶,d’Amico A.⁷,Frongia A. L.²³,Antonaci L.²³,Pirola A.¹^ORCID,Pedemonte M.⁶,Bertini E.⁷^ORCID,Bruno C.⁶,Mercuri E.²³^ORCID,Di Bari Alessandra,Signorino Amelia,Longo Antonella,Tacchetti Paola,Brolatti Noemi,Rossi Diletta,Bravetti Chiara,Lucibello Simona,Fanelli Lavinia,Forcina Nicola,Norcia Giulia,Carnicella Sara,Patanella Katia Agata,Leone Daniela,Palermo Concetta,Berti Beatrice,Catania Felice,Colombo Andrea,Bozzardi Aurora,Ferrantini Gloria,Vita Gianluca,

Affiliation:

1. The NEMO Center in Milan Neurorehabilitation Unit ASST Niguarda Hospital University of Milan MilanItaly

2. Pediatric Neurology Università Cattolica del Sacro Cuore RomeItaly

3. Centro Clinico Nemo Fondazione Policlinico Universitario Agostino Gemelli IRCCS RomeItaly

4. Department of Clinical and Experimental Medicine University of Messina MessinaItaly

5. Nemo SUD Clinical Center University Hospital ‘G. Martino’ MessinaItaly

6. Center of Translational and Experimental Myology IRCCS Istituto Giannina Gaslini GenoaItaly

7. Department of Neurosciences Unit of Neuromuscular and Neurodegenerative Disorders Bambino Gesù Children’s Hospital, IRCCS Rome Italy

Funder

Fondazione Telethon

Publisher

Wiley

Subject

Clinical Neurology,Neurology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/ene.14567

Reference26 articles.

1. Identification and characterization of a spinal muscular atrophy-determining gene

2. Spinal muscular atrophy

3. Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy

4. Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy

5. Feasibility and safety of intrathecal treatment with nusinersen in adult patients with spinal muscular atrophy

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