Assessment of Target Engagement in a First‐in‐Human Trial with Sinbaglustat, an Iminosugar to Treat Lysosomal Storage Disorders-Reference-Cited by-同舟云学术

登录注册会员服务联系我们

Assessment of Target Engagement in a First‐in‐Human Trial with Sinbaglustat, an Iminosugar to Treat Lysosomal Storage Disorders

Published:2020-11-10 Issue:2 Volume:14 Page:558-567
ISSN:1752-8054
Container-title:Clinical and Translational Science
language:en
Short-container-title:Clin Transl Sci

Author:

Gehin Martine¹,Melchior Meggane¹,Welford Richard W.D.²,Sidharta Patricia N.¹,Dingemanse Jasper¹

Affiliation:

1. Clinical Pharmacology Idorsia Pharmaceuticals Ltd Allschwil Switzerland

2. Drug Discovery, Translational Biomarkers Idorsia Pharmaceuticals Ltd Allschwil Switzerland

Publisher

Wiley

Subject

General Pharmacology, Toxicology and Pharmaceutics,General Biochemistry, Genetics and Molecular Biology,General Medicine,General Neuroscience

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/cts.12911

Reference38 articles.

1. Lysosomal Lipid Storage Diseases

2. Lysosomal storage disorders: old diseases, present and future challenges;Klein A.D.;Pediatr. Endocrinol. Rev.,2013

3. Lysosomal storage diseases—the horizon expands

4. Niemann-Pick disease type C

5. Enzyme replacement therapy in patients with Fabry disease: State of the art and review of the literature

Cited by 4 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Flow chemistry based catalytic hydrogenation for improving the synthesis of 1-deoxynojirimycin (DNJ) from an l-sorbose derived precursor;Carbohydrate Research;2023-07

2. In situ glucosylceramide synthesis and its pharmacological inhibition analysed in cells by ¹³ C ₅ ‐sphingosine precursor feeding and mass spectrometry;FEBS Letters;2022-07-13

3. Plasma neurofilament light, glial fibrillary acidic protein and lysosphingolipid biomarkers for pharmacodynamics and disease monitoring of GM2 and GM1 gangliosidoses patients;Molecular Genetics and Metabolism Reports;2022-03

4. Effect of Renal Function Impairment on the Pharmacokinetics, Safety, and Tolerability of the Iminosugar Sinbaglustat;The Journal of Clinical Pharmacology;2021-01-15

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号京ICP备18003416号-3