Therapeutic indications and metabolic effects of metreleptin in patients with lipodystrophy syndromes: Real‐life experience from a national reference network

Author:

Mosbah Héléna12,Vantyghem Marie‐Christine3,Nobécourt Estelle4,Andreelli Fabrizio5,Archambeaud Francoise6,Bismuth Elise7,Briet Claire8,Cartigny Maryse9,Chevalier Benjamin3,Donadille Bruno12,Daguenel Anne10,Fichet Mathilde11,Gautier Jean‐François12,Janmaat Sonja12,Jéru Isabelle12,Legagneur Carole13,Leguier Lysiane3,Maitre Julie14,Mongeois Elise14,Poitou Christine15,Renard Eric16ORCID,Reznik Yves17ORCID,Spiteri Anne18,Travert Florence19,Vergès Bruno20,Zammouri Jamila27,Vigouroux Corinne12ORCID,Vatier Camille12

Affiliation:

1. Endocrinology Department Assistance Publique–Hôpitaux de Paris (AP‐HP), Saint–Antoine University Hospital, National Reference Centre for Rare Diseases of Insulin Secretion and Insulin Sensitivity (PRISIS) Paris France

2. Sorbonne University, Inserm UMR_S 938, Saint–Antoine Research Centre Cardiometabolism and Nutrition University Hospital Institute (ICAN) Paris France

3. Department of Endocrinology, Diabetology and Metabolism, Lille University Hospital; University of Lille, INSERM U1190 European Genomic Institute for Diabetes Lille France

4. Department of Endocrinology, Diabetology and Metabolism La Réunion University Hospital Saint Pierre de la Réunion France

5. AP‐HP, Pitié‐Salpêtrière University Hospital, Department of Diabetology; Sorbonne University, INSERM Nutrition and Obesity: systemic approaches « NutriOmics » Paris France

6. Department of Endocrinology, Diabetology and Metabolism Dupuytren University Hospital Limoges France

7. AP‐HP, Robert‐Debré University Hospital, Department of Paediatric Endocrinology, Diabetology and Metabolism University of Paris Paris France

8. Department of Endocrinology Diabetology and Metabolism, Angers University Hospital, Laboratory MITOVASC, UMR CNRS 6015, INSERM 1083 Angers France

9. Reference Centre for Rare Diseases of Genital Development DEVGEN, Endocrinology Unit, Diabetology and Paediatric Gynecology Department Lille University Hospital Lille France

10. Department of Pharmacy AP‐HP, Saint–Antoine University Hospital Paris France

11. Department of Endocrinology, Diabetology and Metabolism Rennes University Hospital Rennes France

12. Department of Endocrinology, Diabetology and Metabolism AP‐HP, Lariboisière University Hospital Paris France

13. Department of Paediatric Endocrinology, Diabetology and Metabolism University Hospital Brabois‐Vandoeuvre lès Nancy Vandoeuvre lès Nancy France

14. Department of Paediatrics and Endocrinology, Diabetology and Metabolism Orléans Hospital Orléans France

15. Nutrition Department, Sorbonne University/INSERM, Research Unit: Nutrition and Obesity; Systemic Approaches (NutriOmics) AP‐HP, Pitié‐Salpêtrière University Hospital, Reference Centre for Rare Diseases PRADORT (PRADer‐Willi Syndrome and other Rare Obesities with Eating Disorders) Paris France

16. Department of Endocrinology, Diabetes and Nutrition, Montpellier University Hospital; Clinical Investigation Centre INSERM1411; Institute of Functional Genomics, CNRS, INSERM University of Montpellier Montpellier France

17. Department of Endocrinology, Diabetology and Metabolism Côte de Nacre University Hospital Caen France

18. Department of Endocrinology, Diabetology and Metabolism Grenoble University Hospital Grenoble France

19. Department of Diabetology and Metabolism AP‐HP, Bichat University Hospital Paris France

20. Department of Endocrinology, Diabetology and Metabolism Bocage University Hospital Dijon France

Publisher

Wiley

Subject

Endocrinology,Endocrinology, Diabetes and Metabolism,Internal Medicine

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