A golden age for Haemophilia treatment?-Reference-Cited by-同舟云学术

A golden age for Haemophilia treatment?

Published:2018-03 Issue:2 Volume:24 Page:175-176
ISSN:1351-8216
Container-title:Haemophilia
language:en
Short-container-title:Haemophilia

Author:

Makris M.¹²^ORCID,Hermans C.³

Affiliation:

1. Sheffield Haemophilia and Thrombosis Centre; Royal Hallamshire Hospital; Sheffield UK

2. Department of Immunity, Inflammation and Cardiovascular Disease; University of Sheffield; Sheffield UK

3. Haemostasis and Thrombosis Unit; Haemophilia Clinic; Division of Haematology; St-Luc University Hospital; Catholic university of Louvain; Brussels Belgium

Publisher

Wiley

Subject

Genetics(clinical),Hematology,General Medicine

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/hae.13411/fullpdf

Reference8 articles.

1. Interim results from a phase 1/2 AAV5-FVIII gene transfer in patients with severe hemophilia A;Pasi;Int Soc Thromb Haemost,2017

2. Adenovirus-associated virus vector-mediated gene transfer in hemophilia B;Nathwani;N Engl J Med,2011

3. Long-term safety and efficacy of factor IX gene therapy in hemophilia B;Nathwani;N Engl J Med,2014

4. SPK-9001: adeno-associated virus mediated gene transfer for haemophilia B achieved durable endogenous prophylaxis at levels of activity sufficient to achieve significant mean reduction in annual bleeding and infusions rates in preliminary data from an on-going phase 1/2a trial;George;Int Soc Thromb Haemost,2017

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