A model-based approach to assess the exposure-response relationship of Lorenzo's oil in adrenoleukodystrophy-Reference-Cited by-同舟云学术

A model-based approach to assess the exposure-response relationship of Lorenzo's oil in adrenoleukodystrophy

Published:2016-04-03 Issue:6 Volume:81 Page:1058-1066
ISSN:0306-5251
Container-title:British Journal of Clinical Pharmacology
language:en
Short-container-title:Br J Clin Pharmacol

Author:

Ahmed Mariam A.¹²³,Kartha Reena V.¹²,Brundage Richard C.¹²,Cloyd James¹²,Basu Cynthia⁴,Carlin Bradley P.⁴,Jones Richard O.⁵,Moser Ann B.⁶,Fatemi Ali⁷,Raymond Gerald V.⁸

Affiliation:

1. Center for Orphan Drug Research; University of Minnesota; Minneapolis MN

2. Department of Experimental and Clinical Pharmacology; University of Minnesota; Minneapolis MN, USA

3. Department of Pharmacy Practice; Helwan University; Cairo Egypt

4. Division of Biostatistics; University of Minnesota; Minneapolis MN

5. Division of Neurology and Developmental Medicine; Kennedy Krieger Institute; Baltimore MD

6. Peroxisomal Diseases Laboratory; Kennedy Krieger Institute; Baltimore MD

7. Genetics Laboratories; Kennedy Krieger Institute; Baltimore MD

8. Department of Neurology; University of Minnesota; Minneapolis MN USA

Publisher

Wiley

Subject

Pharmacology (medical),Pharmacology

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/bcp.12897/fullpdf

Reference30 articles.

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2. X-linked adrenoleukodystrophy;Aubourg;Ann Endocrinol (Paris),2007

3. Clinical biochemistry of peroxisomal disorders;Kaiser;Clin Chim Acta,1988

4. Adrenoleukodystrophy: a clinical and pathological study of 17 cases;Schaumburg;Arch Neurol,1975

5. X-linked adrenoleukodystrophy: clinical, metabolic, genetic and pathophysiological aspects;Kemp;Biochim Biophys Acta,1822

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