Tafamidis delays neurological progression comparably across Val30Met and non‐Val30Met genotypes in transthyretin familial amyloid polyneuropathy
Author:
Affiliation:
1. InVentiv Health Inc. Burlington MAUSA
2. Pfizer Inc New York NYUSA
3. Pfizer Inc Groton CT USA
Funder
Pfizer
Publisher
Wiley
Subject
Clinical Neurology,Neurology
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1111/ene.13510
Reference17 articles.
1. Update in the diagnosis and management of transthyretin familial amyloid polyneuropathy
2. Temporal trends in transthyretin familial amyloid polyneuropathy survival over a century;Coelho T;Int J Clin Neurosci Ment Health,2016
3. Genotype–phenotype correlation and course of transthyretin familial amyloid polyneuropathies in France
4. THAOS – The Transthyretin Amyloidosis Outcomes Survey: initial report on clinical manifestations in patients with hereditary and wild-type transthyretin amyloidosis
5. Y Sekijima K Yoshida T Tokuda S Ikeda
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