1. New Zealand Organisation for Rare Disorders, Wellington, New Zealand
2. National Centre for Rare Diseases, Istituto Superiore di Sanità, Rome, Italy
3. Fundación GEISER, Mendoza, Argentina
4. Institute of Inborn Errors of Metabolism, Javeriana University, Bogota, Colombia
5. National Organization for Rare Disorders, Washington, DC, USA
6. Shire Human Genetic Therapies, Shire AG, Eysins, Switzerland
7. Childhood Cancer Research Unit, Department of Women’s and Children’s Health, Karolinska Institutet, Karolinska University Hospital Solna, Stockholm, Sweden
8. Haffner Associates, Rockville, MD, USA
9. Promotion Research on Intellectual Property, The University of Tokyo, Tokyo, Japan
10. Research Institute for Rare Diseases, Instituto de Salud Carlos III, Madrid, Spain
11. ABConsult, Leuven, Belgium
12. Office of Rare Diseases Research, National Institutes of Health, Bethesda, MD, USA