New insights in efficacy of different enzyme replacement therapy dosages in Fabry disease: Switch studies data following agalsidase beta shortage-Reference-Cited by-同舟云学术

New insights in efficacy of different enzyme replacement therapy dosages in Fabry disease: Switch studies data following agalsidase beta shortage

Published:2022-11-22 Issue:3 Volume:103 Page:371-376
ISSN:0009-9163
Container-title:Clinical Genetics
language:en
Short-container-title:Clinical Genetics

Author:

Riccio Eleonora¹^ORCID,Pisani Antonio²

Affiliation:

1. Institute for Biomedical Research and Innovation, National Research Council of Italy (IRIB CNR) Palermo Italy

2. Chair of Nephrology, Department of Public Health University Federico II of Naples Naples Italy

Funder

Sanofi

Amicus Therapeutics

Chiesi

Publisher

Wiley

Subject

Genetics (clinical),Genetics

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/cge.14266

Reference7 articles.

1. Switch to agalsidase alfa after shortage of agalsidase beta in Fabry disease: a systematic review and meta-analysis of the literature

2. Switch from agalsidase beta to agalsidase alfa in the enzyme replacement therapy of patients with Fabry disease in Latin America;Ripeau D;Medicina (B Aires),2017

3. Long-Term Dose-Dependent Agalsidase Effects on Kidney Histology in Fabry Disease

4. Treatment switch in Fabry disease- a matter of dose?

5. Fabry disease and enzyme replacement therapy in classic patients with same mutation: different formulations - different outcome?

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1. Clinical outcomes in patients switching from agalsidase beta to migalastat: A Fabry Registry analysis;Journal of Inherited Metabolic Disease;2024-07-04

2. Modern Approach to Fabry Disease Diagnosis and Management in Children;Current Pediatrics;2024-02-25

3. Safety and efficacy of pegunigalsidase alfa in patients with Fabry disease who were previously treated with agalsidase alfa: results from BRIDGE, a phase 3 open-label study;Orphanet Journal of Rare Diseases;2023-10-21

4. Interpretation of GFR slope in untreated and treated adult Fabry patients;Nephrology Dialysis Transplantation;2023-07-13

5. Fabry disease: current treatment and future perspective;Journal of Genetic Medicine;2023-06-30