Gene therapy for primary immunodeficiencies

Author:

Fischer A.1234,Hacein-Bey Abina S.56,Touzot F.1378,Cavazzana M.1378

Affiliation:

1. Paris Descartes - Sorbonne Paris Cité University; Imagine Institute; Paris France

2. Immunology and Pediatric Hematology Department; Assistance Publique-Hôpitaux de Paris; Paris France

3. INSERM UMR 1163; Institut Imagine; Paris France

4. Collège de France; Paris France

5. UTCBS CNRS 8258 - INSERM U1022, Faculté des Sciences Pharmaceutiques et Biologiques; Université Paris Descartes; Paris France

6. Immunology Laboratory; Groupe Hospitalier Universitaire Paris-Sud; Le-Kremlin-Bicêtre France

7. Biotherapy Department, Necker Children's Hospital; Assistance Publique-Hôpitaux de Paris; Paris France

8. Biotherapy Clinical Investigation Center; Groupe Hospitalier Universitaire Ouest, Assistance Publique-Hôpitaux de Paris, INSERM; Paris France

Publisher

Wiley

Subject

Genetics (clinical),Genetics

Reference94 articles.

1. Primary immunodeficiency diseases: an update on the classification from the international union of immunological societies expert committee for primary immunodeficiency;Al-Herz;Front Immunol,2014

2. Gene therapy of severe combined immunodeficiencies;Fischer;Immunol Rev,2000

3. Hazards and potential benefits of blood-transfusion in immunological deficiency;Hong;Lancet,1968

4. Bone-marrow transplantation in a patient with the Wiskott-Aldrich syndrome;Bach;Lancet,1968

5. Transplantation of hematopoietic stem cells and long-term survival for primary immunodeficiencies in Europe: entering a new century, do we do better?;Gennery;J Allergy Clin Immunol,2010

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