A randomized, double‐blind trial of triheptanoin for drug‐resistant epilepsy in glucose transporter 1 deficiency syndrome

Author:

Striano Pasquale12ORCID,Auvin Stéphane34ORCID,Collins Abigail5,Horvath Rita6,Scheffer Ingrid E.7ORCID,Tzadok Michal8,Miller Ian9ORCID,Kay Koenig Mary10,Lacy Adrian11,Davis Ronald12,Garcia‐Cazorla Angela13,Saneto Russell P.14,Brandabur Melanie15,Blair Susan15,Koutsoukos Tony15,De Vivo Darryl16

Affiliation:

1. G. Gaslini Institute, Scientific Institute for Research and Health Care Genoa Italy

2. Departments of Neurosciences, Rehabilitation, Ophthalmology, Genetics, and Maternal and Child Health University of Genoa Genoa Italy

3. Robert Debré University Hospital and University of Paris Paris France

4. University Institute of France Paris France

5. Children’s Hospital Colorado Aurora Colorado USA

6. Department of Clinical Neurosciences University of Cambridge Cambridge UK

7. Austin and Royal Children’s Hospital Florey and Murdoch Institutes University of Melbourne Melbourne Victoria Australia

8. Pediatric Neurology Units Edmond and Lily Safra Children's Hospital Sheba Medical Center, Tel HaShomer Affiliated with the Sackler Faculty of Medicine Tel Aviv University Ramat Gan Israel

9. Miami Children’s Research Institute Miami Florida USA

10. University of Texas Health Science Center at Houston Houston Texas USA

11. Cook Children’s Medical Center Fort Worth Texas USA

12. Neurology and Epilepsy Research Center Pediatric Neurology Orlando Florida USA

13. Sant Joan de Déu Hospital Barcelona Spain

14. Department of Neurology Division of Pediatric Neurology University of Washington/Seattle Children's Hospital Seattle Washington USA

15. Ultragenyx Pharmaceutical Inc Novato California USA

16. Columbia University Irving Medical Center New York New York USA

Funder

Ultragenyx Pharmaceutical

Publisher

Wiley

Subject

Neurology (clinical),Neurology

Cited by 8 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号  京ICP备18003416号-3