The challenges of clinical trials in rare diseases
Author:
Affiliation:
1. St John’s Institute of Dermatology Guy’s and St Thomas’ NHS Foundation Trust Westminster Bridge Road London UK
Publisher
Oxford University Press (OUP)
Subject
Dermatology
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1111/bjd.21686
Reference13 articles.
1. From scientific discovery to treatments for rare diseases – the view from the National Center for Advancing Translational Sciences – Office of Rare Diseases Research;Kaufmann;Orphanet J Rare Dis,2018
2. A checklist for clinical trials in rare disease: obstacles and anticipatory actions – lessons learned from the FOR-DMD trial;Crow;Trials,2018
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