ANZTCT practice statement: sinusoidal obstruction syndrome/veno‐occlusive disease diagnosis and management

Author:

Fleming Shaun1,Scott Ashleigh P.2,Coutsouvelis John34,Fraser Chris5,Bajel Ashish67,Nelson Adam8,Conyers Rachel91011,McEwan Ashley1213ORCID,Yeung David14,Campion Victoria15,Teague Lochie16,McGuire Matthew17,Morris Edward18,Gabriel Melissa19,Wayte Rebecca20,Douglas Genevieve21,Chien Nicole22,Hamad Nada232425ORCID

Affiliation:

1. Clinical Haematology, Alfred Hospital and Australian Centre for Blood Diseases Monash University Melbourne Victoria Australia

2. Department of Haematology and Bone Marrow Transplant Royal Brisbane and Women's Hospital Brisbane Queensland Australia

3. Pharmacy Department Alfred Health Melbourne Victoria Australia

4. Centre for Medicine Use and Safety, Faculty of Pharmacy and Pharmaceutical Sciences Monash University Melbourne Victoria Australia

5. Blood and Marrow Transplant Service, Queensland Children's Hospital Brisbane Queensland Australia

6. Peter MacCallum Cancer Centre and The Royal Melbourne Hospital Melbourne Victoria Australia

7. Faculty of Medicine, Dentistry and Health Sciences University of Melbourne Melbourne Victoria Australia

8. Kids Cancer Centre, Sydney Children's Hospital Sydney New South Wales Australia

9. Pharmacogenomics Team, Stem Cell Biology Murdoch Children's Research Institute Melbourne Victoria Australia

10. Children's Cancer Centre, The Royal Children's Hospital Melbourne Victoria Australia

11. Department of Paediatrics University of Melbourne Melbourne Victoria Australia

12. Haematology Department Liverpool Hospital Sydney New South Wales Australia

13. South West Sydney Clinical School, Faculty of Medicine University of New South Wales Sydney New South Wales Australia

14. Royal Adelaide Hospital and Adelaide Medical School Adelaide South Australia Australia

15. Wellington Blood and Cancer Centre, Wellington Hospital Wellington New Zealand

16. Starship Blood and Cancer Center, Starship Children's Hospital Auckland New Zealand

17. Department of Pharmacy Fiona Stanley Hospital Perth Western Australia Australia

18. Department of Haematology and Bone Marrow Transplantation Townsville University Hospital Townsville Queensland Australia

19. Cancer Centre for Children, The Children's Hospital at Westmead Sydney New South Wales Australia

20. Department of Haematology Royal Prince Alfred Hospital Sydney New South Wales Australia

21. Clinical Haematology, Austin Health Melbourne Victoria Australia

22. Department of Haematology Auckland City Hospital Auckland New Zealand

23. Department of Haematology St Vincent's Hospital Sydney Sydney New South Wales Australia

24. School of Clinical Medicine, Faculty of Medicine and Health UNSW Sydney Sydney New South Wales Australia

25. School of Medicine University of Notre Dame Sydney New South Wales Australia

Abstract

AbstractSinusoidal obstruction syndrome/veno‐occlusive disease (SOS/VOD) is a life‐threatening complication which can develop after haemopoietic stem cell transplantation (HSCT) and some antibody–drug conjugates. Several SOS/VOD diagnostic and management guidelines exist, with the most recent and refined being the European Society for Blood and Marrow Transplantation adult and paediatric guidelines. Timely diagnosis and effective management (including the availability of therapeutic options) significantly contribute to improved patient outcomes. In Australia and New Zealand, there is variability in clinical practice and access to SOS/VOD therapies. This review aims to summarise the current evidence for SOS/VOD diagnosis, prevention and treatment and to provide recommendations for SOS/VOD in the context of contemporary Australasian HSCT clinical practice.

Funder

Pfizer

Publisher

Wiley

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