Affiliation:
1. Hamidiye International School of Medicine University of Health Sciences Istanbul Turkey
Subject
Pharmacology (medical),Pharmacology
Reference6 articles.
1. U.S. Food and Drug Administration. Accessed August 3 2023.https://www.fda.gov/news-events/press-announcements/fda-approves-first-gene-therapy-treatment-certain-patients-duchenne-muscular-dystrophy
2. Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to <8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study SRP‐9001‐103 (ENDEAVOR)
3. FDA approves first gene therapy for Duchenne muscular dystrophy despite internal objections. Accessed August 4 2023.https://www.nature.com/nrd/articles?type=news-in-brief