IDEAL study: A real‐world assessment of pattern of use and clinical outcomes with recombinant coagulation factor IX albumin fusion protein (rIX‐FP) in patients with haemophilia B in Italy-Reference-Cited by-同舟云学术

IDEAL study: A real‐world assessment of pattern of use and clinical outcomes with recombinant coagulation factor IX albumin fusion protein (rIX‐FP) in patients with haemophilia B in Italy

Published:2022-11-24 Issue:1 Volume:29 Page:135-144
ISSN:1351-8216
Container-title:Haemophilia
language:en
Short-container-title:Haemophilia

Author:

Tagliaferri Annarita¹,Molinari Angelo Claudio²^ORCID,Peyvandi Flora³,Coppola Antonio¹^ORCID,Demartis Francesco⁴,Biasoli Chiara⁵,Borchiellini Alessandra⁶,Cultrera Dorina⁷,De Cristofaro Raimondo⁸,Daniele Filomena⁹,Giordano Paola¹⁰,Marchesini Emanuela¹¹,Margaglione Maurizio¹²,Marino Renato¹³,Pollio Berardino¹⁴,Radossi Paolo¹⁵,Santoro Cristina¹⁶^ORCID,Santoro Rita Carlotta¹⁷^ORCID,Siragusa Sergio¹⁸,Sottilotta Gianluca¹⁹^ORCID,Tosetto Alberto²⁰,Piscitelli Lydia²¹,Villa Maria Rosaria²²,Zanon Ezio²³,Finardi Adele²⁴,Schiavetti Irene²⁵²⁶,Vaccari Daniella²⁵,Castaman Giancarlo⁴^ORCID

Affiliation:

1. Regional Reference Centre for Inherited Bleeding Disorders University Hospital of Parma Parma Italy

2. Regional Reference Centre for Haemorrhagic Diseases IRCCS Istituto Giannina Gaslini Genova Italy

3. Department of Pathophysiology and Transplantation Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico Haemophilia and Thrombosis Centre Università degli Studi di Milano Milan Italy

4. Department of Oncology Centre for Bleeding Disorders and Coagulation Careggi University Hospital Florence Italy

5. Haemophilia and Transfusion Centre “Bufalini” Hospital Cesena Italy

6. Regional Reference Centre for Bleeding and Thrombotic Disorders “Città della Salute e della Scienza” University Hospital Turin Italy

7. Haemophilia Regional Reference Centre Haematology Unit Policlinico "G. Rodolico ‐ S. Marco” Hospital Catania Italy

8. Haemorrhagic and Thrombotic Disease Service Area of Haematological and Oncological Sciences IRCCS Fondazione Policlinico Universitario “A. Gemelli” Rome Italy

9. Haemostasis and Thrombosis Service Ospedale Civile dell'Annunziata Cosenza Italy

10. “B. Trambusti” General and Specialised Paediatrics Unit “Giovanni XXIII” Hospital University of Bari Bari Italy

11. Haemophilia Centre, Internal and Cardiovascular Medicine “Santa Maria della Misericordia” University Hospital Perugia Italy

12. Department of Clinical and Experimental Medicine University of Foggia Foggia Italy

13. Haemophilia and Thrombosis Centre University Hospital Bari Italy

14. Regional Reference Centre for Inherited Bleeding and Thrombotic Disorders Transfusion Medicine “Regina Margherita” Children Hospital Turin Italy

15. Onco‐Haematology Unit Istituto Oncologico Veneto Castelfranco Veneto Hospital Castelfranco Veneto Italy

16. Department of Haematology University Hospital Policlinico Umberto I Rome Italy

17. Regional Reference Centre for Haemophilia and Coagulation Diseases Azienda Ospedaliera Pugliese‐Ciaccio Catanzaro Italy

18. Haematology Unit Thrombosis and Haemostasis Reference Regional Centre University of Palermo Palermo Italy

19. Haemophilia Centre Grande Ospedale Metropolitano Reggio Calabria Italy

20. Haematology Department Haemostasis and Thrombosis Unit San Bortolo Hospital Vicenza Italy

21. SSD Congenital Haemorrhagic Diseases IRCCS Azienda Ospedaliero‐Universitaria di Bologna Bologna Italy

22. Haemophilia and Thrombosis Centre Haematology Unit “Ospedale del Mare” Hospital Naples Italy

23. Department of Medicine Haemophilia Centre University Hospital of Padua Padua Italy

24. CSL Behring Milan Italy

25. Hippocrates Research Genova Italy

26. Department of Health Sciences University of Genoa Genoa Italy

Publisher

Wiley

Subject

Genetics (clinical),Hematology,General Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/hae.14689

Reference25 articles.

1. WFH Guidelines for the Management of Hemophilia, 3rd edition

2. Consequences of intra-articular bleeding in haemophilia: science to clinical practice and beyond

3. Optimal treatment strategies for hemophilia: achievements and limitations of current prophylactic regimens

4. Kreuth V initiative: European consensus proposals for treatment of hemophilia using standard products, extended half-life coagulation factor concentrates and non-replacement therapies

5. Genetic fusion to albumin improves the pharmacokinetic properties of factor IX;Metzner HJ;Thromb Haemost,2009

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